Center of Rare Diseases, Section of Medical Pathophysiology, Department of Experimental Medicine, Sapienza University of Rome, Roma, Italy.
Department of Experimental Medicine, Sapienza University of Rome, Roma, Italy.
Clin Exp Immunol. 2021 Sep;205(3):316-325. doi: 10.1111/cei.13616. Epub 2021 Jun 10.
Current literature regarding systemic autoimmune diseases in X-chromosome aneuploidies is scarce and limited to case reports. Our aim was to evaluate the frequency of anti-nuclear (ANAs), extractable nuclear (ENA), anti-double-stranded DNA (dsDNAs), anti-smooth muscle (ASMAs) and anti-mitochondrial (AMAs) antibodies in a large cohort of adults with Klinefelter's syndrome (KS, 47,XXY) and rare higher-grade sex chromosome aneuploidies (HGAs) for the first time. Sera from 138 X-chromosome aneuploid patients [124 adult patients with 47,XXY KS and 14 patients with HGA (six children, eight adults)] and 50 age-matched 46,XY controls were recruited from the Sapienza University of Rome (2007-17) and tested for ANAs, ENAs, anti-dsDNAs, ASMAs and AMAs. Non-organ-specific immunoreactivity was found to be significantly higher in patients with 47,XXY KS (14%) than in the controls (2%, p = 0.002). Among all the antibodies investigated, only ANAs were observed significantly more frequently in patients with 47,XXY KS (12.1%) than in the controls (2%, p = 0.004). No anti-dsDNA immunoreactivity was found. Stratifying by testosterone replacement therapy (TRT), non-organ-specific autoantibody frequencies were higher in TRT-naive (p = 0.01) and TRT-treated groups than in controls. No patients with HGA were found positive for the various autoantibodies. Non-organ-specific autoantibodies were significantly present in 47,XXY adult patients. Conversely, HGAs did not appear to be target of non-organ-specific immunoreactivity, suggesting that KS and HGAs should be considered as two distinct conditions. The classification and diagnosis of systemic autoimmune diseases is frequently difficult. To support a correct clinical evaluation of KS disease and to prevent eventual secondary irreversible immune-mediated damages, we highlight the importance of screening for non-organ-specific autoimmunity in Klinefelter's syndrome.
目前有关 X 染色体非整倍体的系统性自身免疫性疾病的文献很少,且仅限于病例报告。我们的目的是首次评估大量成年克氏综合征(KS,47,XXY)患者和罕见的高等级性染色体非整倍体(HGA)中抗核(ANA)、可提取核(ENA)、抗双链 DNA(dsDNA)、抗平滑肌(ASMA)和抗线粒体(AMA)抗体的频率。从罗马 Sapienza 大学(2007-17 年)招募了 138 名 X 染色体非整倍体患者[124 名成年 47,XXY KS 患者和 14 名 HGA 患者(6 名儿童,8 名成人)]和 50 名年龄匹配的 46,XY 对照者的血清,用于检测 ANA、ENA、抗 dsDNA、ASMA 和 AMA。发现 47,XXY KS 患者(14%)的非器官特异性免疫反应显著高于对照组(2%,p=0.002)。在所研究的所有抗体中,仅在 47,XXY KS 患者中观察到 ANA 明显更为频繁(12.1%),而在对照组中(2%,p=0.004)。未发现抗 dsDNA 免疫反应。按睾酮替代治疗(TRT)分层,TRT 初治(p=0.01)和 TRT 治疗组的非器官特异性自身抗体频率高于对照组。未发现 HGA 患者对各种自身抗体呈阳性。47,XXY 成年患者中存在明显的非器官特异性自身抗体。相反,HGA 似乎不是非器官特异性免疫反应的靶标,这表明 KS 和 HGA 应被视为两种不同的疾病。系统性自身免疫性疾病的分类和诊断常常很困难。为了支持对 KS 疾病的正确临床评估并防止潜在的继发性不可逆免疫介导损伤,我们强调在克氏综合征中筛查非器官特异性自身免疫的重要性。