Plastic Surgery Hospital, Peking Union Medical College and Chinese Academy of Medical Sciences, China.
Plastic Surgery Hospital, Peking Union Medical College and Chinese Academy of Medical Sciences, China.
Stem Cell Res. 2021 May;53:102357. doi: 10.1016/j.scr.2021.102357. Epub 2021 Apr 21.
Congenital microtia is a malformation of the middle and external ear. Duplications involving the ECR, an ear-specific long-range enhancer of HMX1, lead to ear malformation in different species. Use of electroporation of episomal plasmids encodes OCT4, SOX2, NANOG, LIN28, KLF4, and LMYC into peripheral blood mononuclear cells (PBMCs), we generated an induced pluripotent stem cell (iPSCs) line of a microtia patient carrying the duplication involving ECR. The iPSCs express pluripotency markers, have the potential to differentiate into three germ layers, and show the normal karyotype. This patient-specific iPSC will be used for modeling the pathophysiology of ear malformation.
先天性小耳畸形是中耳和外耳的一种畸形。涉及 ECR 的重复,这是 HMX1 的一个特定于耳朵的长程增强子,导致不同物种的耳朵畸形。我们用电穿孔将 OCT4、SOX2、NANOG、LIN28、KLF4 和 LMYC 编码到外周血单核细胞(PBMC)中,生成了一个携带 ECR 重复的小耳畸形患者的诱导多能干细胞(iPSC)系。这些 iPSC 表达多能性标记物,具有分化为三个胚层的潜能,并显示正常核型。这种患者特异性的 iPSC 将用于模拟耳朵畸形的病理生理学。