Frosi Yuri, Ng Simon, Lin Yen-Chu, Jiang Shimin, Ramlan Siti Radhiah, Lama Dilraj, Verma Chandra S, Asial Ignacio, Brown Christopher J
Disease Intervention Technology Lab (DITL), IMCB (ASTAR) 8A Biomedical Grove, #06-04/05, Neuros/Immunos 138648 Singapore
Insilico Medicine Taiwan Ltd. Suite 2013, No. 333, Sec.1, Keelung Rd., Xinyi Dist. 110 Taipei Taiwan.
RSC Chem Biol. 2022 May 19;3(7):916-930. doi: 10.1039/d2cb00099g. eCollection 2022 Jul 6.
Identifying new binding sites and poses that modify biological function are an important step towards drug discovery. We have identified a novel disulphide constrained peptide that interacts with the cap-binding site of eIF4E, an attractive therapeutic target that is commonly overexpressed in many cancers and plays a significant role in initiating a cancer specific protein synthesis program though binding the 5'cap (7'methyl-guanoisine) moiety found on mammalian mRNAs. The use of disulphide constrained peptides to explore intracellular biological targets is limited by their lack of cell permeability and the instability of the disulphide bond in the reducing environment of the cell, loss of which results in abrogation of binding. To overcome these challenges, the cap-binding site interaction motif was placed in a hypervariable loop on an VH domain, and then selections performed to select a molecule that could recapitulate the interaction of the peptide with the target of interest in a process termed Peptide Epitope Linker Evolution (PELE). A novel VH domain was identified that interacted with the eIF4E cap binding site with a nanomolar affinity and that could be intracellularly expressed in mammalian cells. Additionally, it was demonstrated to specifically modulate eIF4E function by decreasing cap-dependent translation and cyclin D1 expression, common effects of eIF4F complex disruption.
识别能够改变生物学功能的新结合位点和构象是药物发现过程中的重要一步。我们鉴定出了一种新型的二硫键约束肽,它与eIF4E的帽结合位点相互作用,eIF4E是一个有吸引力的治疗靶点,在许多癌症中通常过度表达,并且通过结合哺乳动物mRNA上的5'帽(7'-甲基鸟苷)部分,在启动癌症特异性蛋白质合成程序中发挥重要作用。使用二硫键约束肽来探索细胞内生物学靶点受到其细胞通透性不足以及在细胞还原环境中二硫键不稳定的限制,二硫键的丧失会导致结合作用的消除。为了克服这些挑战,将帽结合位点相互作用基序置于VH结构域的高变环中,然后进行筛选,以选择一种能够在一个称为肽表位连接体进化(PELE)的过程中重现肽与目标靶点相互作用的分子。鉴定出了一种新型的VH结构域,它以纳摩尔亲和力与eIF4E帽结合位点相互作用,并且能够在哺乳动物细胞中进行细胞内表达。此外,通过降低帽依赖性翻译和细胞周期蛋白D1表达,证明它能够特异性地调节eIF4E功能,这是eIF4F复合物破坏的常见效应。