Hospita Universitario Gregorio Marañón, Instituto de Investigación Sanitaria Gregorio Marañón, Madrid, Spain.
Hospital Universitario Son Espases, Fundació Institut d'Investigació Sanitària Illes Balears (IdISBa), Palma de Mallorca, Spain.
Front Immunol. 2022 Jul 12;13:855730. doi: 10.3389/fimmu.2022.855730. eCollection 2022.
Real-world evidence comparing the efficacy of chimeric antigen receptor (CAR) T-cell therapy against that of the previous standard of care (SOC) for refractory large B-cell lymphoma (LBCL) is scarce. We retrospectively collected data from patients with LBCL according to SCHOLAR-1 criteria treated with commercial CAR T-cell therapy in Spain (204 patients included and 192 treated, 101 with axicabtagene ciloleucel [axi-cel], and 91 with tisagenlecleucel [tisa-cel]) and compared the results with a historical refractory population of patients (n = 81) obtained from the GELTAMO-IPI study. We observed superior efficacy for CAR-T therapy (for both axi-cel and tisa-cel) over pSOC, with longer progression-free survival (PFS) (median of 5.6 vs. 4-6 months, p ≤ 0.001) and overall survival (OS) (median of 15 vs. 8 months, p < 0.001), independently of other prognostic factors (HR: 0.59 (95% CI: 0.44-0.80); p < 0.001] for PFS, and 0.45 [(95% CI: 0.31-0.64)] for OS). Within the CAR-T cohort, axi-cel showed longer PFS (median of 7.3 versus 2.8 months, respectively, p = 0.027) and OS (58% versus 42% at 12 months, respectively, p = 0.048) than tisa-cel. These differences were maintained in the multivariable analysis. On the other hand, axi-cel was independently associated with a higher risk of severe cytokine release syndrome and neurotoxicity. Our results suggest that the efficacy of CAR-T cell therapy is superior to pSOC in the real-world setting. Furthermore, axi-cel could be superior in efficacy to tisa-cel, although more toxic, in this group of refractory patients according to SCHOLAR-1 criteria.
针对难治性大 B 细胞淋巴瘤(LBCL),比较嵌合抗原受体(CAR)T 细胞疗法与既往标准治疗(SOC)疗效的真实世界证据很少。我们根据 SCHOLAR-1 标准,回顾性地收集了西班牙接受商业 CAR T 细胞治疗的 LBCL 患者的数据(共纳入 204 例患者,192 例接受治疗,101 例接受 axicabtagene ciloleucel [axi-cel]治疗,91 例接受 tisagenlecleucel [tisa-cel]治疗),并将结果与来自 GELTAMO-IPI 研究的难治性患者历史对照人群(n = 81)进行了比较。我们观察到 CAR-T 疗法(axi-cel 和 tisa-cel)对比 pSOC 具有更好的疗效,无进展生存期(PFS)更长(中位 5.6 与 4-6 个月,p ≤ 0.001),总生存期(OS)更长(中位 15 与 8 个月,p < 0.001),与其他预后因素无关(PFS 的风险比 [HR]:0.59(95% CI:0.44-0.80);p < 0.001],OS 的 HR:0.45(95% CI:0.31-0.64))。在 CAR-T 队列中,axi-cel 的 PFS(中位 7.3 与 2.8 个月,p = 0.027)和 OS(58%与 42%,12 个月时,p = 0.048)均长于 tisa-cel。这些差异在多变量分析中得到了维持。另一方面,axi-cel 与严重细胞因子释放综合征和神经毒性的风险增加独立相关。我们的结果表明,在真实世界环境中,CAR-T 细胞疗法的疗效优于 pSOC。此外,根据 SCHOLAR-1 标准,在这组难治性患者中,axi-cel 在疗效上可能优于 tisa-cel,尽管毒性更高。