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AMX0035 和依达拉奉治疗肌萎缩侧索硬化症的有效性和价值:来自临床和经济评价研究所中西部比较有效性公众咨询委员会的总结。

The effectiveness and value of AMX0035 and oral edaravone for amyotrophic lateral sclerosis: A summary from the Institute for Clinical and Economic Review's Midwest Comparative Effectiveness Public Advisory Council.

机构信息

Institute for Clinical and Economic Review, Boston, MA.

Division of Hospital Medicine, San Francisco General Hospital, University of California and Philip R Lee Institute for Health Policy Studies, University of California San Francisco.

出版信息

J Manag Care Spec Pharm. 2023 Feb;29(2):216-221. doi: 10.18553/jmcp.2023.29.2.216.

Abstract

Funding for this summary was contributed by Blue Cross Blue Shield of MA, California Healthcare Foundation, The Patrick and Catherine Weldon Donaghue Medical Research Foundation, Arnold Ventures, and Kaiser Foundation Health Plan Inc., to the Institute for Clinical and Economic Review (ICER), an independent organization that evaluates the evidence on the value of health care interventions. ICER's annual policy summit is supported by dues from Aetna, America's Health Insurance Plans, AbbVie, Alnylam, AstraZeneca, Biogen, Blue Shield of CA, Boehringer Ingelheim, Cambia Health Services, CVS, Editas, Evolve Pharmacy Solutions, Express Scripts, Genentech/ Roche, GlaxoSmithKline, Harvard Pilgrim, Health Care Service Corporation, Health First, Health Partners, Humana, Johnson & Johnson (Janssen), Kaiser Permanente, LEO Pharma, Mallinckrodt, Merck, Novartis, National Pharmaceutical Council, Pfizer. Premera, Prime Therapeutics, Regeneron, Sanofi, Spark Therapeutics, Sun Life Financial, uniQure, and United Healthcare. Mr Nikitin, Ms McKenna, Ms Richardson, and Drs Rind and Pearson are employed by ICER. Through their affiliated institutions, Drs Makam, Carlson, and Suh received funding from ICER for the work described in this summary.

摘要

本摘要的资助由马萨诸塞州蓝十字蓝盾、加州医疗保健基金会、帕特里克和凯瑟琳·韦尔登·多纳休医学研究基金会、阿诺德基金会、凯撒基金会健康计划公司提供给临床和经济评估研究所(ICER),这是一个独立的组织,评估医疗保健干预措施的价值证据。ICER 的年度政策峰会由 Aetna、美国健康保险计划、艾伯维、Alnylam、阿斯利康、百健、加州蓝盾、勃林格殷格翰、Cambia 健康服务、CVS、Editas、Evolve 药房解决方案、Express Scripts、基因泰克/罗氏、葛兰素史克、哈佛朝圣者、医疗保健服务公司、Health First、Health Partners、Humana、强生(杨森)、凯撒 Permanente、利奥制药、美纳里克斯、默克、诺华、国家制药理事会、辉瑞、普雷梅拉、Prime Therapeutics、Regeneron、赛诺菲、Spark Therapeutics、太阳生活金融、uniQure 和联合健康公司赞助。Nikitin 先生、McKenna 女士、Richardson 女士和 Rind 博士和 Pearson 博士受雇于 ICER。通过他们的附属机构,Makam 博士、Carlson 博士和 Suh 博士因本摘要所述工作从 ICER 获得资金。

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