Department of Medical Biochemistry, Max Perutz Labs, Vienna Biocenter, Medical University of Vienna, Vienna, Austria.
Department of Radiation Oncology, Medical University of Vienna, Vienna, Austria.
EMBO Mol Med. 2023 Apr 11;15(4):e17453. doi: 10.15252/emmm.202317453. Epub 2023 Mar 17.
Personalised oncology is at the forefront of cancer research. The goal of personalised oncology is to selectively kill cancer cells while minimising side effects on normal tissue. This can be achieved by identifying and targeting cancer vulnerabilities that distinguish it from normal cells. Many cancers are deficient in high-fidelity DNA repair pathways that maintain genomic stability, such as homologous recombination (HR). Such cancers are highly sensitive to targeted therapies that induce DNA damage or inhibit DNA repair pathways. A notable example and a poster child of personalised oncology are PARP1/2 inhibitors (PARPi) that selectively kill HR-deficient (HRD) cancer cells by preventing repair of DNA gaps or single-strand breaks (SSBs) (Slade, 2020). Inhibitors of cell cycle checkpoints such as CHK1 and WEE1 can also eliminate HRD cancers by pushing cancer cells through the cell cycle despite unrepaired DNA damage and causing death by mitotic catastrophe (Groelly et al, 2022). PARPi have been approved for the treatment of ovarian, breast, pancreatic, and prostate cancer but other cancer types with an HRD signature (HRDness) may also respond to PARPi treatment. Planas-Paz et al (2023) now show that many sarcomas show HRDness and respond to PARP1/2 and WEE1 inhibitors, thus offering a new personalised oncology approach for this treatment-refractory cancer.
个性化肿瘤学处于癌症研究的前沿。个性化肿瘤学的目标是选择性地杀死癌细胞,同时将对正常组织的副作用降到最低。这可以通过识别和靶向癌症弱点来实现,这些弱点将其与正常细胞区分开来。许多癌症缺乏维持基因组稳定性的高保真 DNA 修复途径,例如同源重组 (HR)。此类癌症对靶向治疗高度敏感,这些治疗会诱导 DNA 损伤或抑制 DNA 修复途径。PARP1/2 抑制剂 (PARPi) 就是一个显著的例子,它是个性化肿瘤学的代表药物,通过阻止 DNA 缺口或单链断裂 (SSBs) 的修复,选择性地杀死 HR 缺陷 (HRD) 癌细胞(Slade,2020)。细胞周期检查点抑制剂,如 CHK1 和 WEE1,也可以通过在存在未修复的 DNA 损伤的情况下推动癌细胞通过细胞周期,从而消除 HRD 癌症,并通过有丝分裂灾难导致细胞死亡(Groelly 等人,2022)。PARPi 已被批准用于治疗卵巢癌、乳腺癌、胰腺癌和前列腺癌,但具有 HRD 特征(HRDness)的其他癌症类型也可能对 PARPi 治疗有反应。Planas-Paz 等人(2023)现在表明,许多肉瘤具有 HRDness 并对 PARP1/2 和 WEE1 抑制剂有反应,因此为这种治疗难治性癌症提供了一种新的个性化肿瘤学方法。