细胞特刊：“视网膜疾病的分子和细胞基础”。
Cells Special Issue: "The Molecular and Cellular Basis of Retinal Diseases".
机构信息
Department of Optometry and Vision Science, Vision Science Research Center, School of Optometry, University of Alabama at Birmingham, Birmingham, AL 35294-0019, USA.
Departments of Ophthalmology and Biochemistry and Neuroscience Graduate Program, Jacobs School of Medicine and Biomedical Sciences, The State University of New York-University at Buffalo, Buffalo, NY 14203-1121, USA.
出版信息
Cells. 2023 Jul 26;12(15):1933. doi: 10.3390/cells12151933.
Abstract
The recent success in the treatment of hereditary retinal disease caused by defects in the RPE65 gene and the FDA approval of this treatment has established the importance of the study of animal models and the translational impact of these research findings [...].
摘要
最近在治疗由 RPE65 基因突变引起的遗传性视网膜疾病方面取得的成功，以及美国食品和药物管理局对该治疗方法的批准，都确立了研究动物模型的重要性，以及这些研究结果的转化意义。
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