Department of Biomedical Engineering, Boston University.
Institute for Medical Engineering and Science, Massachusetts Institute of Technology.
J Vis Exp. 2023 Dec 8(202). doi: 10.3791/66189.
Creating synthetic biomarkers for the development of precision diagnostics has enabled detection of disease through pathways beyond those used for traditional biofluid measurements. Synthetic biomarkers generally make use of reporters that provide readable signals in the biofluid to reflect the biochemical alterations in the local disease microenvironment during disease incidence and progression. The pharmacokinetic concentration of the reporters and biochemical amplification of the disease signal are paramount to achieving high sensitivity and specificity in a diagnostic test. Here, a cancer diagnostic platform is built using one format of synthetic biomarkers: activity-based nanosensors carrying chemically stabilized DNA reporters that can be liberated by aberrant proteolytic signatures in the tumor microenvironment. Synthetic DNA as a disease reporter affords multiplexing capability through its use as a barcode, allowing for the readout of multiple proteolytic signatures at once. DNA reporters released into the urine are detected using CRISPR nucleases via hybridization with CRISPR RNAs, which in turn produce a fluorescent or colorimetric signal upon enzyme activation. In this protocol, DNA-barcoded, activity-based nanosensors are constructed and their application is exemplified in a preclinical mouse model of metastatic colorectal cancer. This system is highly modifiable according to disease biology and generates multiple disease signals simultaneously, affording a comprehensive understanding of the disease characteristics through a minimally invasive process requiring only nanosensor administration, urine collection, and a paper test which enables point-of-care diagnostics.
创建用于开发精准诊断的合成生物标志物使得能够通过传统生物流体测量所使用的途径之外的途径来检测疾病。合成生物标志物通常利用在生物流体中提供可读信号的报告器来反映疾病发生和进展过程中局部疾病微环境中的生化改变。报告器的药代动力学浓度和疾病信号的生化放大对于在诊断测试中实现高灵敏度和特异性至关重要。在这里,使用一种合成生物标志物的格式构建了癌症诊断平台:带有化学稳定化 DNA 报告器的基于活性的纳米传感器,这些报告器可以通过肿瘤微环境中的异常蛋白水解特征被释放。作为疾病报告器的合成 DNA 通过用作条形码提供了多重分析能力,允许同时读取多个蛋白水解特征。通过与 CRISPR RNA 杂交,使用 CRISPR 核酸酶检测释放到尿液中的 DNA 报告器,然后在酶激活时产生荧光或比色信号。在本方案中,构建了带有 DNA 条形码的基于活性的纳米传感器,并在转移性结直肠癌的临床前小鼠模型中举例说明了它们的应用。根据疾病生物学,该系统具有高度可修饰性,并同时产生多个疾病信号,通过仅需要纳米传感器给药、尿液收集和纸测试的微创过程,全面了解疾病特征,从而实现即时诊断。