Precision medicine in action for Pompe disease.
作者信息
Tarallo Antonietta, Parenti Giancarlo, Brunetti-Pierri Nicola
机构信息
Department of Translational Medicine, Section of Pediatrics, University of Naples Federico II, Naples, Italy.
Telethon Institute of Genetics and Medicine, Pozzuoli, Italy.
出版信息
Mol Ther Nucleic Acids. 2024 Jul 9;35(3):102265. doi: 10.1016/j.omtn.2024.102265. eCollection 2024 Sep 10.
Abstract
摘要
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