Bautista-Sanchez Rocio, Khanna Dinesh
Division of Rheumatology, University of Michigan, Ann Arbor, MI, Michigan USA.
Scleroderma Program, University of Michigan, Ann Arbor, MI, Michigan USA.
Rheumatol Immunol Res. 2024 Oct 21;5(3):157-165. doi: 10.2478/rir-2024-0022. eCollection 2024 Sep.
Systemic sclerosis (SSc) or scleroderma is an autoimmune disease characterized by immune dysregulation which leads to progressive fibrosis of the skin and internal organs. Interstitial lung disease (ILD) is present in approximately 65% of patients with SSc and it accounts for approximately 40% of all SSc deaths. Risk factors associated with the development of systemic sclerosis related interstitial lung disease (SSc-ILD) include male sex, African heritage, high modified Rodnan skin score (mRSS), presence of anti-Scl-70/Topoisomerase I antibodies, and nucleolar pattern on antinuclear antibody (ANA). The primary tool to diagnose ILD in patients with SSc is high-resolution computed tomography (HRCT). Full pulmonary function tests (PFTs) with diffusing capacity of the lungs for carbon monoxide (DLco) and ambulatory desaturation testing should be obtained following the diagnosis of SSc-ILD for disease monitoring. The purpose of this review is to provide an updated guide for the management of SSc-ILD. Our proposed first line treatment for SSc-ILD is immunosuppressive therapy such as mycophenolate mofetil, tocilizumab, and rituximab which are discussed in depth, and we present the evidence-based data that has justified the use of these pharmacotherapies. Other immunosuppressive treatments are also reviewed, and we discuss the role of antifibrotic therapy. Finally, we dive into other avenues of treatments such as chimeric antigen receptor (CAR)-T cell therapy and hematopoietic stem cell transplant.
系统性硬化症(SSc)或硬皮病是一种自身免疫性疾病,其特征是免疫失调,可导致皮肤和内脏进行性纤维化。间质性肺疾病(ILD)在大约65%的SSc患者中存在,约占所有SSc死亡病例的40%。与系统性硬化症相关的间质性肺疾病(SSc-ILD)发生相关的危险因素包括男性、非洲裔、改良Rodnan皮肤评分(mRSS)高、抗Scl-70/拓扑异构酶I抗体阳性以及抗核抗体(ANA)的核仁型。诊断SSc患者ILD的主要工具是高分辨率计算机断层扫描(HRCT)。在诊断SSc-ILD后,应进行包括肺一氧化碳弥散量(DLco)的全面肺功能测试(PFTs)和动态血氧饱和度测试,以监测疾病。本综述的目的是为SSc-ILD的管理提供最新指南。我们提议的SSc-ILD一线治疗是免疫抑制治疗,如霉酚酸酯、托珠单抗和利妥昔单抗,我们将对其进行深入讨论,并展示支持使用这些药物治疗的循证数据。还对其他免疫抑制治疗进行了综述,并讨论了抗纤维化治疗的作用。最后,我们深入探讨了其他治疗途径,如嵌合抗原受体(CAR)-T细胞疗法和造血干细胞移植。