Ahsanuddin Sofia, Wu Albert Y
Department of Ophthalmology, Byers Eye Institute, Stanford University School of Medicine, Stanford, CA, USA.
Department of Ophthalmology, Icahn School of Medicine at Mount Sinai, New York City, NY, USA.
Taiwan J Ophthalmol. 2023 Oct 20;14(4):554-564. doi: 10.4103/tjo.TJO-D-23-00096. eCollection 2024 Oct-Dec.
Thyroid eye disease (TED) is a poorly understood autoimmune condition affecting the retroorbital tissue. Tissue inflammation, expansion, and fibrosis can potentially lead to debilitating sequelae such as vision loss, painful eye movement, proptosis, and eyelid retraction. Current treatment modalities for TED include systemic glucocorticoids, thioamides, methimazole, teprotumumab, beta-blockers, and radioactive iodine; however, it has been reported that up to 10%-20% of TED patients relapse after treatment withdrawal and 20%-30% are unresponsive to mainstay therapy for reasons that have yet to be more clearly elucidated. In the past 4 years, vision researchers have harnessed high-throughput single-cell RNA sequencing to elucidate the diversity of cell types and molecular mechanisms driving the pathogenesis of TED at single-cell resolution. Such studies have provided unprecedented insight regarding novel biomarkers and therapeutic targets in TED. This timely review summarizes recent breakthroughs and emerging opportunities for using single-cell and single-nuclei transcriptomic data to characterize this highly complex disease state. We also provide an overview of current challenges and future applications of this technology to potentially improve patient quality of life and facilitate reversal of disease endpoints.
甲状腺眼病(TED)是一种人们了解甚少的自身免疫性疾病,会影响眶后组织。组织炎症、增生和纤维化可能会导致视力丧失、眼球运动疼痛、眼球突出和眼睑退缩等使人衰弱的后遗症。目前TED的治疗方式包括全身性糖皮质激素、硫代酰胺、甲巯咪唑、替普罗单抗、β受体阻滞剂和放射性碘;然而,据报道,高达10%-20%的TED患者在停药后会复发,20%-30%的患者对主流治疗无反应,原因尚未完全阐明。在过去4年里,视觉研究人员利用高通量单细胞RNA测序技术,以单细胞分辨率阐明了驱动TED发病机制的细胞类型多样性和分子机制。这类研究为TED中的新型生物标志物和治疗靶点提供了前所未有的见解。这篇及时的综述总结了利用单细胞和单细胞核转录组数据来描述这种高度复杂疾病状态的最新突破和新出现的机会。我们还概述了该技术当前面临的挑战以及未来的应用,这些应用有可能改善患者的生活质量并促进疾病终点的逆转。