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Response and Adverse Event Rates With Placebo in Compensated MASH-related Cirrhosis: A Meta-analysis.

作者信息

Amaral Marcio J M, Moura Felipe S, Lima Luan C V, Souza Matheus

机构信息

Department of Internal Medicine, Federal University of Rio de Janeiro, Rio de Janeiro, Brazil.

出版信息

J Clin Exp Hepatol. 2025 May-Jun;15(3):102487. doi: 10.1016/j.jceh.2024.102487. Epub 2024 Dec 16.

DOI:10.1016/j.jceh.2024.102487
PMID:40458254
原文链接:https://pmc.ncbi.nlm.nih.gov/articles/PMC12126923/
Abstract
摘要

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本文引用的文献

1
A roadmap for clinical trials in MASH-related compensated cirrhosis.MASH 相关代偿性肝硬化临床试验路线图。
Nat Rev Gastroenterol Hepatol. 2024 Nov;21(11):809-823. doi: 10.1038/s41575-024-00955-8. Epub 2024 Jul 17.
2
Resmetirom: First Approval.雷美替胺:首次获批
Drugs. 2024 Jun;84(6):729-735. doi: 10.1007/s40265-024-02045-0. Epub 2024 May 21.
3
A Phase 3, Randomized, Controlled Trial of Resmetirom in NASH with Liver Fibrosis.一项评估 Resmetirom 治疗伴有肝纤维化的 NASH 的 3 期随机对照试验。
N Engl J Med. 2024 Feb 8;390(6):497-509. doi: 10.1056/NEJMoa2309000.
4
A randomized, double-blind, placebo-controlled trial of aldafermin in patients with NASH and compensated cirrhosis.一项在伴有 NASH 和代偿性肝硬化的患者中进行的aldafermin 的随机、双盲、安慰剂对照试验。
Hepatology. 2024 Mar 1;79(3):674-689. doi: 10.1097/HEP.0000000000000607. Epub 2023 Sep 21.
5
Pegbelfermin in Patients With Nonalcoholic Steatohepatitis and Compensated Cirrhosis (FALCON 2): A Randomized Phase 2b Study.佩格司他丁治疗非酒精性脂肪性肝炎和代偿性肝硬化患者(FALCON 2):一项随机 2b 期研究。
Clin Gastroenterol Hepatol. 2024 Jan;22(1):113-123.e9. doi: 10.1016/j.cgh.2023.04.012. Epub 2023 Apr 23.
6
Semaglutide 2·4 mg once weekly in patients with non-alcoholic steatohepatitis-related cirrhosis: a randomised, placebo-controlled phase 2 trial.每周一次给予 2.4 毫克司美格鲁肽治疗非酒精性脂肪性肝炎相关肝硬化患者:一项随机、安慰剂对照的 2 期临床试验。
Lancet Gastroenterol Hepatol. 2023 Jun;8(6):511-522. doi: 10.1016/S2468-1253(23)00068-7. Epub 2023 Mar 16.
7
Challenges and opportunities in NASH drug development.非酒精性脂肪性肝炎药物研发的挑战与机遇。
Nat Med. 2023 Mar;29(3):562-573. doi: 10.1038/s41591-023-02242-6. Epub 2023 Mar 9.
8
A randomized, double-blind, placebo-controlled phase IIa trial of efruxifermin for patients with compensated NASH cirrhosis.一项针对代偿性非酒精性脂肪性肝炎肝硬化患者的efruxifermin随机、双盲、安慰剂对照IIa期试验。
JHEP Rep. 2022 Aug 23;5(1):100563. doi: 10.1016/j.jhepr.2022.100563. eCollection 2023 Jan.
9
Placebo Adverse Events in Non-alcoholic Steatohepatitis Clinical Trials: A Pooled Analysis of 2,944 Participants.安慰剂不良反应在非酒精性脂肪性肝炎临床试验中的分析:2944 名参与者的汇总分析。
Am J Gastroenterol. 2023 Apr 1;118(4):645-653. doi: 10.14309/ajg.0000000000002042. Epub 2022 Sep 30.
10
Placebo effect on progression and regression in NASH: Evidence from a meta-analysis.安慰剂效应对 NASH 进展和缓解的影响:来自荟萃分析的证据。
Hepatology. 2022 Jun;75(6):1647-1661. doi: 10.1002/hep.32315. Epub 2022 Jan 24.