Mansfield Christopher R, Taggart Elizabeth L, Chirgwin Michael E, Derbyshire Emily R
Department of Chemistry, Duke University, Durham, NC, USA; Department of Molecular Genetics & Microbiology, Duke Medical School, Durham, NC, USA.
Department of Chemistry, Duke University, Durham, NC, USA.
Bioorg Med Chem. 2025 Aug 26;130:118371. doi: 10.1016/j.bmc.2025.118371.
The molecular chaperone heat shock protein 90 (Hsp90) has an important role in maintaining proteostasis in Plasmodium parasites, the causative agents of malaria, and is of interest as a potential antimalarial drug target. Inhibitors targeting its well-characterized N-terminal ATP-binding site are lethal, but the development of high-affinity binders with selectivity for the Plasmodium over the human homolog has been challenging given the high conservation of this domain. A binding site in the less conserved Hsp90 C-terminus has been reported to interact with nucleotides and inhibitors in other eukaryotic systems, which could offer an alternative route for antimalarial design. Herein, we characterize the potential ligandability of the C-terminus in the Plasmodium falciparum chaperone PfHsp90 with in silico and in vitro methods. We conducted affinity experiments with both a lysine-reactive nucleotide analog and an ATP resin that support a specific interaction between ATP and a C-terminal truncation of PfHsp90. We further explored the nucleotide structural requirements for this interaction with limited proteolysis experiments, which suggest association with ATP, dATP, and ADP, but not AMP or GTP. Lastly, we employed computational analyses and mutagenesis studies to interrogate the molecular basis for the interaction. Our findings provide the foundation for future studies to assess and develop C-terminal Hsp90 inhibitors against Plasmodium parasites.
分子伴侣热休克蛋白90(Hsp90)在维持疟原虫(疟疾的病原体)的蛋白质稳态中起着重要作用,并且作为潜在的抗疟药物靶点备受关注。靶向其特征明确的N端ATP结合位点的抑制剂具有致死性,但鉴于该结构域的高度保守性,开发对疟原虫比对人类同源物具有选择性的高亲和力结合剂一直具有挑战性。据报道,在其他真核生物系统中,保守性较低的Hsp90 C端的一个结合位点可与核苷酸和抑制剂相互作用,这可能为抗疟药物设计提供一条替代途径。在此,我们用计算机模拟和体外方法表征了恶性疟原虫伴侣蛋白PfHsp90 C端的潜在可配体性。我们用赖氨酸反应性核苷酸类似物和ATP树脂进行了亲和力实验,这些实验支持ATP与PfHsp90 C端截短体之间的特异性相互作用。我们通过有限蛋白酶解实验进一步探索了这种相互作用的核苷酸结构要求,实验结果表明其与ATP、dATP和ADP相关,但与AMP或GTP无关。最后,我们采用计算分析和诱变研究来探究这种相互作用的分子基础。我们的研究结果为未来评估和开发针对疟原虫的C端Hsp90抑制剂的研究奠定了基础。