Budarf M L, Emanuel B S
Division of Human Genetics and Molecular Biology, The Children's Hospital of Philadelphia, PA 19104, USA.
Hum Mol Genet. 1997;6(10):1657-65. doi: 10.1093/hmg/6.10.1657.
Based on cytogenetic observations, several syndromes have been previously identified as microdeletion-based disorders. In this review, recent progress is presented regarding whether one or multiple genes can be implicated in the pathogenesis of these segmentally aneusomic syndromes. The syndromes discussed include Angelman, Alagille, Williams, Langer-Giedeon, Prader-Willi, Smith-Magenis, Miller-Dieker, and DiGeorge/velocardiofacial or the 22q11 deletion syndromes. For Angelman and Alagille syndromes, single genes have been identified, whereas for Williams and Langer-Giedion syndromes, more than one gene can be implicated. Although there has been significant progress in dissecting the molecular basis for the other disorders, the ultimate answer regarding one versus several genes remains to be determined.
基于细胞遗传学观察,先前已将几种综合征确定为基于微缺失的疾病。在本综述中,介绍了关于一个或多个基因是否可能与这些节段性非整倍体综合征的发病机制有关的最新进展。所讨论的综合征包括天使综合征、阿拉吉列综合征、威廉姆斯综合征、朗格-吉迪恩综合征、普拉德-威利综合征、史密斯-马吉尼斯综合征、米勒-迪克尔综合征以及迪乔治/心脏颜面综合征或22q11缺失综合征。对于天使综合征和阿拉吉列综合征,已鉴定出单个基因,而对于威廉姆斯综合征和朗格-吉迪恩综合征,则可能涉及多个基因。尽管在剖析其他疾病的分子基础方面取得了重大进展,但关于是一个基因还是几个基因的最终答案仍有待确定。