Dip. Sc. Mediche e Chirurgiche-DIMEC, U.O. Genetica Medica, Policlinico Universitario S.Orsola-Malpighi, Bologna, Italy.
Eur J Hum Genet. 2013 Oct;21(10):1169-72. doi: 10.1038/ejhg.2013.8. Epub 2013 Feb 6.
Birt-Hogg-Dubè (BHD) is an autosomal dominant syndrome characterised by skin fibrofolliculomas, lung cysts, spontaneous pneumothorax and renal cancer. The association of benign cutaneous lesions and increased cancer risk is also a feature of Cowden Syndrome (CS), an autosomal dominant disease caused by PTEN mutations. BHD and CS patients may develop oncocytomas, rare neoplasias that are phenotypically characterised by a prominent mitochondrial hyperplasia. We here describe the genetic analysis of a parotid and a thyroid oncocytoma, developed by a BHD and a CS patient, respectively. The BHD lesion was shown to maintain the wild-type allele of FLCN, while losing one PTEN allele. On the other hand, a double heterozygosity for the same two genes was found to be the only detectable tumorigenic hit in the CS oncocytoma. Both conditions occurred in a context of high chromosomal stability, as highlighted by comparative genomic hybridisation analysis. We conclude that, similarly to PTEN, FLCN may not always follow the classical Two Hits model of tumorigenesis and may hence belong to a class of non-canonical tumour suppressor genes. We hence introduce a role of PTEN/FLCN double heterozygosity in syndromic oncocytic tumorigenesis, suggesting this to be an alternative determinant to pathogenic mitochondrial DNA mutations, which are instead the genetic hallmark of sporadic oncocytic tumours.
Birt-Hogg-Dubé (BHD) 是一种常染色体显性综合征,其特征为皮肤纤维毛囊瘤、肺囊肿、自发性气胸和肾癌。良性皮肤病变和癌症风险增加的关联也是 Cowden 综合征 (CS) 的特征,CS 是一种常染色体显性疾病,由 PTEN 突变引起。BHD 和 CS 患者可能会发展为嗜酸细胞瘤,这是一种罕见的肿瘤,其表型特征为明显的线粒体增生。我们在这里描述了由 BHD 和 CS 患者分别发展的腮腺和甲状腺嗜酸细胞瘤的遗传分析。BHD 病变显示保持 FLCN 的野生型等位基因,而失去一个 PTEN 等位基因。另一方面,在 CS 嗜酸细胞瘤中发现了这两个基因的双杂合性是唯一可检测到的肿瘤发生性打击。这两种情况都发生在高染色体稳定性的背景下,如比较基因组杂交分析所强调的那样。我们得出结论,与 PTEN 相似,FLCN 可能并不总是遵循经典的肿瘤发生的“两次打击”模型,因此可能属于一类非经典的肿瘤抑制基因。我们因此引入了 PTEN/FLCN 双杂合性在综合征性嗜酸细胞瘤发生中的作用,表明这是一种替代致病性线粒体 DNA 突变的决定因素,而后者是散发性嗜酸细胞瘤的遗传标志。