Biswas Swati, Arun Banu, Parmigiani Giovanni
Department of Mathematical Sciences, University of Texas at Dallas, Richardson, TX 75080-3021, U.S.A.
Stat Med. 2014 May 20;33(11):1914-27. doi: 10.1002/sim.6077. Epub 2013 Dec 18.
Risk prediction models play an important role in prevention and treatment of several diseases. Models that are in clinical use are often refined and improved. In many instances, the most efficient way to improve a successful model is to identify subgroups for which there is a specific biological rationale for improvement and tailor the improved model to individuals in these subgroups, an approach especially in line with personalized medicine. At present, we lack statistical tools to evaluate improvements targeted to specific subgroups. Here, we propose simple tools to fill this gap. First, we extend a recently proposed measure, the Integrated Discrimination Improvement, using a linear model with covariates representing the subgroups. Next, we develop graphical and numerical tools that compare reclassification of two models, focusing only on those subjects for whom the two models reclassify differently. We apply these approaches to BRCAPRO, a genetic risk prediction model for breast and ovarian cancer, using data from MD Anderson Cancer Center. We also conduct a simulation study to investigate properties of the new reclassification measure and compare it with currently used measures. Our results show that the proposed tools can successfully uncover subgroup specific model improvements.
风险预测模型在多种疾病的预防和治疗中发挥着重要作用。临床使用的模型通常会不断完善和改进。在许多情况下,改进一个成功模型的最有效方法是识别那些有特定生物学依据可改进的亚组,并针对这些亚组中的个体调整改进后的模型,这种方法特别符合个性化医疗。目前,我们缺乏评估针对特定亚组改进情况的统计工具。在此,我们提出了一些简单工具来填补这一空白。首先,我们使用一个带有代表亚组协变量的线性模型,扩展了最近提出的一种度量方法——综合鉴别改进。接下来,我们开发了图形和数值工具,用于比较两个模型的重新分类情况,只关注那些两个模型重新分类不同的受试者。我们将这些方法应用于BRCAPRO,这是一种用于乳腺癌和卵巢癌的遗传风险预测模型,使用了来自MD安德森癌症中心的数据。我们还进行了一项模拟研究,以调查新的重新分类度量方法的特性,并将其与目前使用的度量方法进行比较。我们的结果表明,所提出的工具能够成功揭示亚组特异性的模型改进情况。