Suri Megha, Soni Nitin, Okpaleke Nkiruka, Yadav Shikha, Shah Suchitra, Iqbal Zafar, Alharbi Mohammed G, Kalra Harjeevan S, Hamid Pousette
Medicine-Pediatrics, California Institute of Behavioral Neurosciences & Psychology, Fairfield, USA.
Medicine, California Institute of Behavioral Neurosciences & Psychology, Fairfield, USA.
Cureus. 2021 Sep 28;13(9):e18349. doi: 10.7759/cureus.18349. eCollection 2021 Sep.
Osteosarcoma (OS) is the most common primary bone cancer affecting children and young adults, most often occurring at the metaphysis of long bones. At present, treatment with combinations of surgery and chemotherapy for the localized OS has only brought minuscule improvements in prognosis. In comparison, the advanced, metastatic, or recurrent forms of OS are often non-responsive to chemotherapy, adding to the dire need to develop new and efficient therapies. The question of interest investigated in this systematic review is whether immunotherapy can play a meaningful role in improving the clinical outcomes of children with OS. This article aims to summarize the preclinical and clinical research conducted thus far on potential therapeutic avenues for pediatric OS using immunotherapy, including methods like checkpoint inhibition, adoptive cellular therapy with T-cells, chimeric antigen receptor T (CAR-T), and natural killer (NK) cells. It also highlights the influence of the innate and adaptive immune system on the tumor microenvironment, allowing for OS progression and metastasis. This systematic review contains 27 articles and analyses of multiple clinical trials employing immunotherapeutic drugs to 785 osteosarcoma participants and over 243 pediatric patients. The articles were obtained through PubMed, PubMed Central, and ClinicalTrials.gov and individually assessed for quality using the Assessment of Multiple Systematic Reviews (AMSTAR) checklist and the Cochrane risk-of-bias tool. The reviews reveal that immunotherapy's most significant impact on pediatric OS includes combining immune checkpoint blockers with traditional chemotherapy and surgery. However, due to the bimodal distribution of this aggressive malignancy, these studies cannot precisely estimate the overall effect and any potential life-threatening adverse events following therapy in children. Further research is required to fully assess the impact of these immunotherapies, including more extensive multinational clinical trials to focus on the pediatric population.
骨肉瘤(OS)是影响儿童和年轻人的最常见原发性骨癌,最常发生于长骨的干骺端。目前,针对局限性骨肉瘤采用手术和化疗联合治疗,在预后方面仅带来了微小的改善。相比之下,晚期、转移性或复发性骨肉瘤通常对化疗无反应,这更迫切需要开发新的有效疗法。本系统评价所研究的问题是免疫疗法能否在改善骨肉瘤患儿的临床结局方面发挥有意义的作用。本文旨在总结迄今为止关于使用免疫疗法治疗小儿骨肉瘤潜在治疗途径的临床前和临床研究,包括检查点抑制、T细胞过继性细胞疗法、嵌合抗原受体T(CAR-T)细胞和自然杀伤(NK)细胞等方法。文章还强调了先天性和适应性免疫系统对肿瘤微环境的影响,这种影响促进了骨肉瘤的进展和转移。本系统评价纳入了27篇文章,并分析了多项使用免疫治疗药物治疗785例骨肉瘤参与者和243例以上儿科患者的临床试验。这些文章通过PubMed、PubMed Central和ClinicalTrials.gov获取,并使用多重系统评价评估(AMSTAR)清单和Cochrane偏倚风险工具对每篇文章的质量进行单独评估。评价结果显示,免疫疗法对小儿骨肉瘤最显著的影响包括将免疫检查点阻断剂与传统化疗和手术相结合。然而,由于这种侵袭性恶性肿瘤的双峰分布,这些研究无法精确估计总体疗效以及治疗后儿童可能出现的任何危及生命的不良事件。需要进一步研究以全面评估这些免疫疗法的影响,包括开展更广泛的针对儿科人群的多国临床试验。