Department of Biological Sciences, Lehigh University, Bethlehem, PA 18015, USA.
G3 (Bethesda). 2022 Feb 4;12(2). doi: 10.1093/g3journal/jkab426.
Roberts syndrome (RBS) is a multispectrum developmental disorder characterized by severe limb, craniofacial, and organ abnormalities and often intellectual disabilities. The genetic basis of RBS is rooted in loss-of-function mutations in the essential N-acetyltransferase ESCO2 which is conserved from yeast (Eco1/Ctf7) to humans. ESCO2/Eco1 regulate many cellular processes that impact chromatin structure, chromosome transmission, gene expression, and repair of the genome. The etiology of RBS remains contentious with current models that include transcriptional dysregulation or mitotic failure. Here, we report evidence that supports an emerging model rooted in defective DNA damage responses. First, the results reveal that redox stress is elevated in both eco1 and cohesion factor Saccharomyces cerevisiae mutant cells. Second, we provide evidence that Eco1 and cohesion factors are required for the repair of oxidative DNA damage such that ECO1 and cohesin gene mutations result in reduced cell viability and hyperactivation of DNA damage checkpoints that occur in response to oxidative stress. Moreover, we show that mutation of ECO1 is solely sufficient to induce endogenous redox stress and sensitizes mutant cells to exogenous genotoxic challenges. Remarkably, antioxidant treatment desensitizes eco1 mutant cells to a range of DNA damaging agents, raising the possibility that modulating the cellular redox state may represent an important avenue of treatment for RBS and tumors that bear ESCO2 mutations.
罗伯茨综合征(RBS)是一种多谱发育障碍,其特征为严重的肢体、颅面和器官异常,并且通常存在智力障碍。RBS 的遗传基础源于必需的 N-乙酰转移酶 ESCO2 的功能丧失突变,ESCO2 从酵母(Eco1/Ctf7)到人类都是保守的。ESCO2/Eco1 调节许多影响染色质结构、染色体传递、基因表达和基因组修复的细胞过程。RBS 的病因仍然存在争议,目前的模型包括转录失调或有丝分裂失败。在这里,我们报告了支持新兴模型的证据,该模型植根于有缺陷的 DNA 损伤反应。首先,结果表明,氧化还原应激在 eco1 和黏合因子 Saccharomyces cerevisiae 突变细胞中都升高。其次,我们提供的证据表明,Eco1 和黏合因子是修复氧化 DNA 损伤所必需的,因此 ECO1 和黏合基因的突变导致细胞活力降低和对氧化应激的 DNA 损伤检查点的过度激活。此外,我们表明,ECO1 的突变足以诱导内源性氧化还原应激,并使突变细胞对细胞外遗传毒性挑战敏感。值得注意的是,抗氧化剂治疗使 eco1 突变细胞对一系列 DNA 损伤剂脱敏,这表明调节细胞氧化还原状态可能是治疗 RBS 和携带 ESCO2 突变的肿瘤的重要途径。