Kuchukulla Ratnakar Reddy, Hwang Injeoung, Park Sang Won, Moon Sojeong, Kim Suhn Hyung, Kim Sumin, Chung Hwan Won, Ji Mi-Jung, Park Hyun-Mee, Kong Gu, Hur Wooyoung
HY-KIST Bioconvergence, Hanyang University, 222 Wangsimniro, Seongdong-gu, Seoul 04763, Korea.
Medicinal Materials Research Center, Korea Institute of Science and Technology (KIST), 5 Hwarangro 14 Gil, Seongbuk-gu, Seoul 02792, Korea.
Pharmaceuticals (Basel). 2022 Aug 23;15(9):1041. doi: 10.3390/ph15091041.
HER2-positive (HER2+) breast cancer is defined by HER2 oncogene amplification on chromosome 17q12 and accounts for 15−20% population of breast-cancer patients. Therapeutic anti-HER2 antibody such as trastuzumab is used as the first-line therapy for HER2-positive breast cancers. However, more than 50% of the patients respond poorly to trastuzumab, illustrating that novel therapy is warranted to overcome the resistance. We previously reported that in the majority of HER2+ breast-cancer patients, CDK12 is co-amplified on 17q12 and involved in developing tumors and trastuzumab resistance, proposing CDK12 as a potential drug target for HER2+ breast cancers. Here, we designed and synthesized novel 2,6,9-trisubstituted purines as potent CDK12 inhibitors showing strong, equipotent antiproliferative activity against trastuzumab-sensitive HER2+ SK-Br3 cells and trastuzumab-resistant HER2+ HCC1954 cells (GI50 values < 50 nM) both of which express a high level of CDK12. Two potent analogue 30d and 30e at 40, 200 nM greatly downregulated the levels of cyclinK and Pol II p-CTD (Ser2), as well as the expression of CDK12 downstream genes (IRS1 and WNT1) in a dose-dependent manner. We also observed structure-property relationship for a subset of potent analogues, and found that 30e is highly stable in liver microsomes with lack of CYP inhibition. In addition, 30d exhibited a synergy with trastuzumab in the both cells, suggesting that our inhibitors could be applied to alleviate trastuzumab-resistance of HER2+ breast cancers and escalate the efficacy of trastuzumab as well. Our study may provide insight into developing a novel therapy for HER2+ breast cancers.
人表皮生长因子受体2阳性(HER2+)乳腺癌是由17号染色体长臂12区(17q12)上的HER2癌基因扩增所定义的,占乳腺癌患者群体的15%-20%。治疗性抗HER2抗体,如曲妥珠单抗,被用作HER2阳性乳腺癌的一线治疗药物。然而,超过50%的患者对曲妥珠单抗反应不佳,这表明需要新的治疗方法来克服耐药性。我们之前报道,在大多数HER2+乳腺癌患者中,细胞周期蛋白依赖性激酶12(CDK12)在17q12上共同扩增,并参与肿瘤发生和曲妥珠单抗耐药,提示CDK12是HER2+乳腺癌的一个潜在药物靶点。在此,我们设计并合成了新型的2,6,9-三取代嘌呤作为有效的CDK12抑制剂,对曲妥珠单抗敏感的HER2+ SK-Br3细胞和曲妥珠单抗耐药的HER2+ HCC1954细胞均显示出强大且等效的抗增殖活性(半数生长抑制浓度[GI50]值<50 nM),这两种细胞均高表达CDK12。两种有效的类似物30d和30e在40、200 nM时以剂量依赖性方式显著下调细胞周期蛋白K(cyclinK)和RNA聚合酶II羧基末端结构域磷酸化丝氨酸2(Pol II p-CTD)的水平,以及CDK12下游基因(胰岛素受体底物1[IRS1]和Wnt信号通路成员1[WNT1])的表达。我们还观察了一部分有效类似物的构效关系,发现30e在肝微粒体中高度稳定且无细胞色素P450(CYP)抑制作用。此外,30d在两种细胞中均与曲妥珠单抗表现出协同作用,表明我们的抑制剂可用于减轻HER2+乳腺癌的曲妥珠单抗耐药性,并提高曲妥珠单抗的疗效。我们的研究可能为开发HER2+乳腺癌的新疗法提供思路。