Department of Biology, University of Rome Tor Vergata, Via Della Ricerca Scientifica, 00133, Rome, Italy.
Human Technopole, Viale Rita Levi-Montalcini 1, 20157, Milan, Italy.
Mol Psychiatry. 2024 Jan;29(1):186-196. doi: 10.1038/s41380-023-02317-3. Epub 2023 Dec 15.
Autism spectrum disorder (ASD) comprises a large group of neurodevelopmental conditions featuring, over a wide range of severity and combinations, a core set of manifestations (restricted sociality, stereotyped behavior and language impairment) alongside various comorbidities. Common and rare variants in several hundreds of genes and regulatory regions have been implicated in the molecular pathogenesis of ASD along a range of causation evidence strength. Despite significant progress in elucidating the impact of few paradigmatic individual loci, such sheer complexity in the genetic architecture underlying ASD as a whole has hampered the identification of convergent actionable hubs hypothesized to relay between the vastness of risk alleles and the core phenotypes. In turn this has limited the development of strategies that can revert or ameliorate this condition, calling for a systems-level approach to probe the cross-talk of cooperating genes in terms of causal interaction networks in order to make convergences experimentally tractable and reveal their clinical actionability. As a first step in this direction, we have captured from the scientific literature information on the causal links between the genes whose variants have been associated with ASD and the whole human proteome. This information has been annotated in a computer readable format in the SIGNOR database and is made freely available in the resource website. To link this information to cell functions and phenotypes, we have developed graph algorithms that estimate the functional distance of any protein in the SIGNOR causal interactome to phenotypes and pathways. The main novelty of our approach resides in the possibility to explore the mechanistic links connecting the suggested gene-phenotype relations.
自闭症谱系障碍 (ASD) 包含一大组神经发育障碍,其特征是在广泛的严重程度和组合中,存在一组核心表现(社交受限、刻板行为和语言障碍)以及各种合并症。在自闭症的发病机制中,数百个基因和调控区域的常见和罕见变异与一系列因果证据强度有关。尽管在阐明少数典型个体基因座的影响方面取得了显著进展,但自闭症整体遗传结构的复杂性使得难以确定假设在大量风险等位基因和核心表型之间传递的收敛可操作枢纽。反过来,这也限制了可以逆转或改善这种情况的策略的发展,需要采用系统级方法来探测合作基因之间的串扰,以在因果相互作用网络方面进行实验,从而使收敛具有可操作性,并揭示其临床可操作性。作为朝这个方向迈出的第一步,我们从科学文献中捕获了与 ASD 相关的基因变体和整个人类蛋白质组之间因果关系的信息。这些信息已在 SIGNOR 数据库中以计算机可读格式进行注释,并在资源网站上免费提供。为了将这些信息与细胞功能和表型联系起来,我们开发了图算法,该算法可以估计 SIGNOR 因果互作网络中任何蛋白质与表型和途径的功能距离。我们方法的主要新颖之处在于可以探索连接建议的基因-表型关系的机制联系。