The Walter and Eliza Hall Institute of Medical Research, Parkville, VIC, Australia.
Department of Medical Biology, University of Melbourne, Parkville, VIC, Australia.
Nat Commun. 2024 Jul 23;15(1):6219. doi: 10.1038/s41467-024-50566-9.
Papain-like protease (PLpro) is an attractive drug target for SARS-CoV-2 because it is essential for viral replication, cleaving viral poly-proteins pp1a and pp1ab, and has de-ubiquitylation and de-ISGylation activities, affecting innate immune responses. We employ Deep Mutational Scanning to evaluate the mutational effects on PLpro enzymatic activity and protein stability in mammalian cells. We confirm features of the active site and identify mutations in neighboring residues that alter activity. We characterize residues responsible for substrate binding and demonstrate that although residues in the blocking loop are remarkably tolerant to mutation, blocking loop flexibility is important for function. We additionally find a connected network of mutations affecting activity that extends far from the active site. We leverage our library to identify drug-escape variants to a common PLpro inhibitor scaffold and predict that plasticity in both the S4 pocket and blocking loop sequence should be considered during the drug design process.
木瓜蛋白酶样蛋白酶(PLpro)是 SARS-CoV-2 的一个有吸引力的药物靶点,因为它对病毒复制至关重要,可切割病毒多聚蛋白 pp1a 和 pp1ab,具有去泛素化和去 ISG 化活性,影响先天免疫反应。我们采用深度突变扫描技术来评估对哺乳动物细胞中 PLpro 酶活性和蛋白质稳定性的突变影响。我们确认了活性位点的特征,并确定了改变活性的相邻残基的突变。我们表征了负责底物结合的残基,并证明尽管阻塞环中的残基对突变具有惊人的耐受性,但阻塞环的灵活性对于功能很重要。此外,我们还发现了一个影响活性的突变的连接网络,该网络远远超出了活性部位。我们利用我们的文库来鉴定对常见 PLpro 抑制剂支架的药物逃逸变体,并预测在药物设计过程中应考虑 S4 口袋和阻塞环序列的可塑性。