Pagano Gennaro, Monnet Annabelle, Reyes Adriana, Ribba Benjamin, Svoboda Hanno, Kustermann Thomas, Simuni Tanya, Postuma Ronald B, Pavese Nicola, Stocchi Fabrizio, Brockmann Kathrin, Smigorski Krzysztof, Gerbaldo Valentina, Fontoura Paulo, Doody Rachelle, Kerchner Geoffrey A, Brundin Patrik, Marek Kenneth, Bonni Azad, Nikolcheva Tania
Roche Pharma Research and Early Development (pRED), Neuroscience and Rare Diseases Discovery and Translational Area, Roche Innovation Center Basel, Basel, Switzerland.
University of Exeter Medical School, London, UK.
Nat Med. 2024 Dec;30(12):3669-3675. doi: 10.1038/s41591-024-03270-6. Epub 2024 Oct 8.
The Phase II trial of Anti-alpha-Synuclein Antibody in Early Parkinson's Disease (PASADENA) is an ongoing double-blind, placebo-controlled trial evaluating the safety and efficacy of prasinezumab in early-stage Parkinson's disease (PD). During the double-blind period, prasinezumab-treated individuals showed less progression of motor signs (Movement Disorders Society-sponsored revision of the Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Part III) than placebo-treated individuals. We evaluated whether the effect of prasinezumab on motor progression, assessed as a change in MDS-UPDRS Part III score in the OFF and ON states, and MDS-UPDRS Part II score, was sustained for 4 years from the start of the trial. We compared participants enrolled in the PASADENA open-label extension study with those enrolled in an external comparator arm derived from the Parkinson's Progression Markers Initiative observational study. The PASADENA delayed-start (n = 94) and early-start (n = 177) groups showed a slower decline (a smaller increase in score) in MDS-UPDRS Part III scores in the OFF state (delayed start, -51%; early start, -65%), ON state (delayed start, -94%; early start, -118%) and MDS-UPDRS Part II (delayed start, -48%; early start, -40%) than did the Parkinson's Progression Markers Initiative external comparator (n = 303). This exploratory analysis, which requires confirmation in future studies, suggested that the effect of prasinezumab in slowing motor progression in PD may be sustained long term. PASADENA ClinicalTrials.gov no. NCT03100149 .
抗α-突触核蛋白抗体治疗早期帕金森病(PASADENA)的II期试验是一项正在进行的双盲、安慰剂对照试验,旨在评估普拉克索单抗在早期帕金森病(PD)中的安全性和有效性。在双盲期,接受普拉克索单抗治疗的个体运动症状进展(运动障碍协会赞助修订的统一帕金森病评定量表(MDS-UPDRS)第三部分)比接受安慰剂治疗的个体更少。我们评估了普拉克索单抗对运动进展的影响,以关期和开期MDS-UPDRS第三部分评分的变化以及MDS-UPDRS第二部分评分来评估,从试验开始起是否持续了4年。我们将参加PASADENA开放标签扩展研究的参与者与参加帕金森病进展标志物倡议观察性研究的外部对照臂的参与者进行了比较。PASADENA延迟启动组(n = 94)和早期启动组(n = 177)在关期(延迟启动组,-51%;早期启动组,-65%)、开期(延迟启动组,-94%;早期启动组,-118%)和MDS-UPDRS第二部分(延迟启动组,-48%;早期启动组,-40%)的MDS-UPDRS第三部分评分下降(评分增加较小)比帕金森病进展标志物倡议外部对照(n = 303)更慢。这项探索性分析需要在未来研究中得到证实,表明普拉克索单抗在减缓PD运动进展方面的作用可能是长期持续的。PASADENA临床试验注册号:NCT03100149 。