Zhu Shun, Travis Sue M, Elcock Adrian H
Department of Biochemistry, University of Iowa, Iowa City, IA 52242.
J Chem Theory Comput. 2013 Jul 9;9(7):3151-3164. doi: 10.1021/ct400104x.
A major current challenge for drug design efforts focused on protein kinases is the development of drug resistance caused by spontaneous mutations in the kinase catalytic domain. The ubiquity of this problem means that it would be advantageous to develop fast, effective computational methods that could be used to determine the effects of potential resistance-causing mutations before they arise in a clinical setting. With this long-term goal in mind, we have conducted a combined experimental and computational study of the thermodynamic effects of active-site mutations on a well-characterized and high-affinity interaction between a protein kinase and a small-molecule inhibitor. Specifically, we developed a fluorescence-based assay to measure the binding free energy of the small-molecule inhibitor, SB203580, to the p38α MAP kinase and used it measure the inhibitor's affinity for five different kinase mutants involving two residues (Val38 and Ala51) that contact the inhibitor in the crystal structure of the inhibitor-kinase complex. We then conducted long, explicit-solvent thermodynamic integration (TI) simulations in an attempt to reproduce the experimental relative binding affinities of the inhibitor for the five mutants; in total, a combined simulation time of 18.5 μs was obtained. Two widely used force fields - OPLS-AA/L and Amber ff99SB-ILDN - were tested in the TI simulations. Both force fields produced excellent agreement with experiment for three of the five mutants; simulations performed with the OPLS-AA/L force field, however, produced qualitatively incorrect results for the constructs that contained an A51V mutation. Interestingly, the discrepancies with the OPLS-AA/L force field could be rectified by the imposition of position restraints on the atoms of the protein backbone and the inhibitor without destroying the agreement for other mutations; the ability to reproduce experiment depended, however, upon the strength of the restraints' force constant. Imposition of position restraints in corresponding simulations that used the Amber ff99SB-ILDN force field had little effect on their ability to match experiment. Overall, the study shows that both force fields can work well for predicting the effects of active-site mutations on small molecule binding affinities and demonstrates how a direct combination of experiment and computation can be a powerful strategy for developing an understanding of protein-inhibitor interactions.
当前,针对蛋白激酶的药物设计工作面临的一个主要挑战是激酶催化结构域中的自发突变导致的耐药性问题。这个问题的普遍性意味着开发快速、有效的计算方法将具有重要意义,这些方法可用于在临床环境中潜在的耐药性突变出现之前确定其影响。出于这个长期目标,我们对活性位点突变对蛋白激酶与小分子抑制剂之间充分表征且具有高亲和力的相互作用的热力学效应进行了实验与计算相结合的研究。具体而言,我们开发了一种基于荧光的测定方法来测量小分子抑制剂SB203580与p38α丝裂原活化蛋白激酶的结合自由能,并使用该方法测量抑制剂对五个不同激酶突变体的亲和力,这些突变体涉及抑制剂 - 激酶复合物晶体结构中与抑制剂接触的两个残基(Val38和Ala51)。然后,我们进行了长时间的显式溶剂热力学积分(TI)模拟,试图重现抑制剂对这五个突变体的实验相对结合亲和力;总共获得了18.5微秒的组合模拟时间。在TI模拟中测试了两个广泛使用的力场——OPLS - AA/L和Amber ff99SB - ILDN。对于五个突变体中的三个,这两个力场都与实验结果达成了极好的一致性;然而,使用OPLS - AA/L力场进行的模拟对于包含A51V突变的构建体产生了定性错误的结果。有趣的是,通过对蛋白质主链原子和抑制剂施加位置约束,可以纠正与OPLS - AA/L力场的差异,而不会破坏其他突变的一致性;然而,重现实验结果的能力取决于约束的力常数强度。在使用Amber ff99SB - ILDN力场的相应模拟中施加位置约束对其与实验匹配的能力影响很小。总体而言,该研究表明这两个力场在预测活性位点突变对小分子结合亲和力的影响方面都能很好地发挥作用,并展示了实验与计算的直接结合如何能够成为深入理解蛋白质 - 抑制剂相互作用的有力策略。