Department of Microbiology, Immunology and Molecular Genetics, University of California, Los Angeles, CA, 90095, USA.
Department of Ophthalmology, University of California, San Diego, La Jolla, CA, 92093, USA.
Sci Rep. 2018 Jun 14;8(1):9122. doi: 10.1038/s41598-018-27228-0.
African trypanosomes, Trypanosoma brucei spp., are lethal pathogens that cause substantial human suffering and limit economic development in some of the world's most impoverished regions. The name Trypanosoma ("auger cell") derives from the parasite's distinctive motility, which is driven by a single flagellum. However, despite decades of study, a requirement for trypanosome motility in mammalian host infection has not been established. LC1 is a conserved dynein subunit required for flagellar motility. Prior studies with a conditional RNAi-based LC1 mutant, RNAi-K/R, revealed that parasites with defective motility could infect mice. However, RNAi-K/R retained residual expression of wild-type LC1 and residual motility, thus precluding definitive interpretation. To overcome these limitations, here we generate constitutive mutants in which both LC1 alleles are replaced with mutant versions. These double knock-in mutants show reduced motility compared to RNAi-K/R and are viable in culture, but are unable to maintain bloodstream infection in mice. The virulence defect is independent of infection route but dependent on an intact host immune system. By comparing different mutants, we also reveal a critical dependence on the LC1 N-terminus for motility and virulence. Our findings demonstrate that trypanosome motility is critical for establishment and maintenance of bloodstream infection, implicating dynein-dependent flagellar motility as a potential drug target.
非洲锥虫,即布氏锥虫 spp.,是致命的病原体,会给人类带来巨大痛苦,并限制世界上一些最贫困地区的经济发展。锥虫(“打孔细胞”)这个名称源于寄生虫独特的运动方式,这种运动方式由单个鞭毛驱动。然而,尽管经过了几十年的研究,仍未确定锥虫在哺乳动物宿主感染中的运动能力是必需的。LC1 是一种保守的动力蛋白亚基,是鞭毛运动所必需的。以前使用条件性 RNAi 基因为 LC1 突变体,即 RNAi-K/R 的研究表明,运动能力有缺陷的寄生虫可以感染小鼠。然而,RNAi-K/R 仍然表达野生型 LC1 和残留的运动能力,因此无法做出明确的解释。为了克服这些限制,我们在这里生成了 LC1 两个等位基因都被突变版本取代的组成型突变体。与 RNAi-K/R 相比,这些双敲入突变体的运动能力降低,在培养物中仍然存活,但无法在小鼠中维持血流感染。这种毒力缺陷与感染途径无关,但依赖于完整的宿主免疫系统。通过比较不同的突变体,我们还揭示了 LC1 N 端对于运动和毒力的关键依赖性。我们的发现表明,锥虫的运动能力对于建立和维持血流感染至关重要,这表明依赖于动力蛋白的鞭毛运动可能是一个潜在的药物靶点。