Normandie University, UNIROUEN, INSERM U1234, Rouen, France.
Normandie University, UNIROUEN, Rouen University Hospital, Department of Dermatology, French reference center for autoimmune bullous diseases, F76000, Rouen, France.
Sci Rep. 2019 Mar 5;9(1):3525. doi: 10.1038/s41598-019-40203-7.
Bullous Pemphigoid is the most common auto-immune bullous skin disease. It is characterized by the production of auto-antibodies directed against 2 proteins of the hemi-desmosome (BP180 and BP230). We assessed the efficacy and mechanisms of action of rituximab, an anti-CD20 monoclonal antibody, in 17 patients with severe and relapsing type of bullous pemphigoid. The phenotype, cytokine gene expression, and rearrangement of BP180-specific B-cell receptor genes were performed over 2 years following treatment. At the end of the study, 5 patients had died, 3 had withdrawn from the study, and 9 patients were in complete remission. The one- and two-year relapse rates were 44.1% (95% Confidence Interval (CI): 21.0-76.0%) and 66.5%, (95% CI: 38.4-91.4%), respectively. Phenotypic analyses confirmed dramatic B-cell depletion, which lasted for 9 to 12 months. The ELISA values of serum anti-BP180 antibodies and the frequency of BP180-specific circulating B cells decreased dramatically following treatment, which paralleled the improvement of skin lesions. During B-cell reconstitution, a polyclonal IgM repertoire appeared and a shift in the rearrangement of the B-cell receptor genes of BP180-specific circulating B cells was observed. Concurrently, we observed a decrease of IL-15, IL-6 and TNFα expressing BP180-specific B cells, and the emergence of IL-10 and IL-1RA-expressing BP180-specific IgM+ B cells in patients in complete remission off therapy, suggesting the functional plasticity of BP180-specific auto-immune B cells after rituximab treatment.
大疱性类天疱疮是最常见的自身免疫性大疱性皮肤病。它的特征是产生针对半桥粒 2 种蛋白(BP180 和 BP230)的自身抗体。我们评估了利妥昔单抗(一种抗 CD20 单克隆抗体)在 17 例严重和复发性大疱性类天疱疮患者中的疗效和作用机制。在治疗后 2 年内,对患者的表型、细胞因子基因表达和 BP180 特异性 B 细胞受体基因重排进行了评估。研究结束时,5 例患者死亡,3 例患者退出研究,9 例患者完全缓解。1 年和 2 年的复发率分别为 44.1%(95%置信区间:21.0-76.0%)和 66.5%(95%置信区间:38.4-91.4%)。表型分析证实了剧烈的 B 细胞耗竭,这种耗竭持续了 9 至 12 个月。治疗后,血清抗 BP180 抗体的 ELISA 值和 BP180 特异性循环 B 细胞的频率均显著下降,与皮肤病变的改善相平行。在 B 细胞重建过程中,出现了多克隆 IgM 谱,并且 BP180 特异性循环 B 细胞的 B 细胞受体基因重排发生了转变。同时,我们观察到在完全缓解的患者中,IL-15、IL-6 和 TNFα 表达的 BP180 特异性 B 细胞减少,而 IL-10 和 IL-1RA 表达的 BP180 特异性 IgM+B 细胞出现,这表明利妥昔单抗治疗后 BP180 特异性自身免疫 B 细胞的功能可塑性。