Rauf Shahzad, Almas Talal, Ullah Irfan, Usman Norina, Irfan Muhammad
Pediatrics, Khyber Teaching Hospital, Peshawar, PAK.
Internal Medicine, Royal College of Surgeons in Ireland, Dublin, IRL.
Cureus. 2020 Aug 12;12(8):e9706. doi: 10.7759/cureus.9706.
Maple syrup urine disease, an inherited disorder of metabolism, is characterised by deficient activity of the branched-chain alpha-keto acid dehydrogenase complex (BCKAD) enzyme, resulting in an accumulation of branched-chain amino acids. While it is classically diagnosed by the means of a neonatal screening panel, it can sometimes remain undetected. In such cases, maple syrup urine disease is noted to elicit a constellation of clinical symptoms characterised by a plethora of neurological and respiratory impairments. A prompt diagnosis and management of the disease therefore remains imperative. Due to the remarkable semblance in the clinical symptoms elicited by maple syrup urine disease and urea cycle disorders, both the ailments should be considered in the list of differential diagnosis in patients presenting with elevated serum ammonia levels in the context of the overarching clinical picture. We chronicle the case of a 25-day-old neonate who presented with unabated seizures. An initial diagnosis of a urea cycle disorder was suspected; however, further diagnostic workup divulged an underlying diagnosis of maple syrup urine disease.
枫糖尿症是一种遗传性代谢紊乱疾病,其特征是支链α-酮酸脱氢酶复合体(BCKAD)酶活性不足,导致支链氨基酸积累。虽然传统上通过新生儿筛查进行诊断,但有时仍可能未被发现。在这种情况下,枫糖尿症会引发一系列临床症状,其特征是出现大量神经和呼吸功能障碍。因此,对该疾病进行及时诊断和治疗仍然至关重要。由于枫糖尿症和尿素循环障碍所引发的临床症状极为相似,在综合临床情况下血清氨水平升高的患者的鉴别诊断清单中,这两种疾病都应被考虑在内。我们记录了一名25天大的新生儿出现持续性癫痫发作的病例。最初怀疑是尿素循环障碍;然而,进一步的诊断检查揭示了潜在的枫糖尿症诊断。