Department of Dermatology, School of Medicine, Yale University, New Haven, CT 06520.
Department of Biomedical Engineering, School of Engineering and Applied Science, Yale University, New Haven, CT 06511.
Proc Natl Acad Sci U S A. 2021 Feb 16;118(7). doi: 10.1073/pnas.2020575118.
Keratinocyte-derived carcinomas, including squamous cell carcinoma (SCC), comprise the most common malignancies. Surgical excision is the therapeutic standard but is not always clinically feasible, and currently available alternatives are limited to superficial tumors. To address the need for a nonsurgical treatment for nodular skin cancers like SCC, we developed a bioadhesive nanoparticle (BNP) drug delivery system composed of biodegradable polymer, poly(lactic acid)-hyperbranched polyglycerol (PLA-HPG), encapsulating camptothecin (CPT). Nanoparticles (NPs) of PLA-HPG are nonadhesive NPs (NNPs), which are stealthy in their native state, but we have previously shown that conversion of the vicinal diols of HPG to aldehydes conferred NPs the ability to form strong covalent bonds with amine-rich surfaces. Herein, we show that these BNPs have significantly enhanced binding to SCC tumor cell surfaces and matrix proteins, thereby significantly enhancing the therapeutic efficacy of intratumoral drug delivery. Tumor injection of BNP-CPT resulted in tumor retention of CPT at ∼50% at 10 d postinjection, while CPT was undetectable in NNP-CPT or free (intralipid) CPT-injected tumors at that time. BNP-CPT also significantly reduced tumor burden, with a portion (∼20%) of BNP-CPT-treated established tumors showing histologic cure. Larger, more fully established PDV SCC tumors treated with a combination of BNP-CPT and immunostimulating CpG oligodeoxynucleotides exhibited enhanced survival relative to controls, revealing the potential for BNP delivery to be used along with local tumor immunotherapy. Taken together, these results indicate that percutaneous delivery of a chemotherapeutic agent via BNPs, with or without adjuvant immunostimulation, represents a viable, nonsurgical alternative for treating cutaneous malignancy.
角朊细胞来源的癌,包括鳞状细胞癌(SCC),构成了最常见的恶性肿瘤。手术切除是治疗标准,但并非在所有临床情况下都可行,目前可用的替代方法仅限于浅层肿瘤。为了满足对 SCC 等结节性皮肤癌的非手术治疗需求,我们开发了一种由可生物降解聚合物聚乳酸-超支化聚甘油(PLA-HPG)组成的生物粘附纳米颗粒(BNP)药物递送系统,该系统包封喜树碱(CPT)。PLA-HPG 的纳米颗粒(NPs)是无粘性 NPs(NNPs),在其天然状态下是隐形的,但我们之前已经表明,HPG 的顺式二醇转化为醛赋予 NPs 与富含胺的表面形成强共价键的能力。在此,我们表明这些 BNPs 与 SCC 肿瘤细胞表面和基质蛋白的结合能力显著增强,从而显著增强了肿瘤内药物递送的治疗效果。肿瘤内注射 BNP-CPT 导致肿瘤在注射后 10 天内保留 CPT 约 50%,而在此时,NNP-CPT 或游离(Intralipid)CPT 注射的肿瘤中则无法检测到 CPT。BNP-CPT 还显著降低了肿瘤负担,部分(约 20%)经 BNP-CPT 治疗的已建立 PDV SCC 肿瘤显示出组织学治愈。与对照组相比,联合使用 BNP-CPT 和免疫刺激 CpG 寡脱氧核苷酸治疗更大、更完全建立的 PDV SCC 肿瘤,显示出更好的生存能力,这表明 BNPs 递送与局部肿瘤免疫治疗联合使用的潜力。总之,这些结果表明,通过 BNPs 经皮递送电化疗药物,无论是否联合辅助免疫刺激,都是治疗皮肤恶性肿瘤的可行的非手术替代方法。