Laboratory of Functional Biology (LFBio), Center for Cell-Based Therapy (CTC), Regional Blood Center of Ribeirão Preto, Rua Tenente Catão Roxo, 2501, Ribeirão Preto, SP, CEP: 14051-140, Brazil.
Department of Genetics, Ribeirao Preto Medical School, University of São Paulo (FMRP-USP), Ribeirão Preto, SP, Brazil.
Stem Cell Res Ther. 2019 Jan 11;10(1):24. doi: 10.1186/s13287-018-1124-6.
Thoroughly understanding the molecular mechanisms responsible for the biological properties of pluripotent stem cells, as well as for the processes involved in reprograming, differentiation, and transition between Naïve and Primed pluripotent states, is of great interest in basic and applied research. Although pluripotent cells have been extensively characterized in terms of their transcriptome and miRNome, a comprehensive understanding of how these gene products specifically impact their biology, depends on gain- or loss-of-function experimental approaches capable to systematically interrogate their function. We review all studies carried up to date that used arrayed screening approaches to explore the function of these genetic elements on those biological contexts, using focused or genome-wide genetic libraries. We further discuss the limitations and advantages of approaches based on assays with population-level primary readouts, derived from single-parameter plate readers, or cell-level primary readouts, obtained using multiparametric flow cytometry or quantitative fluorescence microscopy (i.e., high-content screening). Finally, we discuss technical limitation and future perspectives, highlighting how the integration of screening data may lead to major advances in the field of stem cell research and therapy.
深入理解多能干细胞生物学特性以及重编程、分化和原始态与起始态之间转变所涉及的分子机制,在基础和应用研究中具有重要意义。尽管多能细胞在转录组和miRNome 方面已经得到了广泛的描述,但要全面了解这些基因产物如何特异性地影响其生物学功能,还需要依赖于能够系统地研究其功能的获得或丧失功能的实验方法。我们回顾了迄今为止所有使用基因芯片筛选方法来研究这些遗传元件在这些生物学背景下功能的研究,这些研究使用了靶向或全基因组的遗传文库。我们进一步讨论了基于具有群体水平原始读数的测定法的优缺点,这些原始读数来自于单参数板读数器,或使用多参数流式细胞术或定量荧光显微镜获得的细胞水平原始读数(即高通量筛选)。最后,我们讨论了技术限制和未来展望,强调了筛选数据的整合如何可能引领干细胞研究和治疗领域的重大进展。