Department of Molecular Medicine, The Scripps Research Institute, La Jolla, California, USA.
Department of Ophthalmology, Juntendo University School of Medicine, Tokyo, Japan.
JCI Insight. 2020 Jun 18;5(12):137317. doi: 10.1172/jci.insight.137317.
Abnormal subretinal neovascularization is a characteristic of vision-threatening retinal diseases, including macular telangiectasia (MacTel) and retinal angiomatous proliferation (RAP). Subretinal neovascular tufts and photoreceptor dysfunction are observed in very-low-density lipoprotein receptor (Vldlr-/-) mutant mice. These changes mirror those observed in patients with MacTel and RAP, but the pathogenesis is largely unknown. In this study, we show that retinal microglia were closely associated with retinal neovascular tufts in Vldlr-/- mice and retinal tissue from patients with MacTel; ablation of microglia/macrophages dramatically prevented formation of retinal neovascular tufts and improved neuronal function, as assessed by electroretinography. Vldlr-/- mice with retinal pigmented epithelium-specific (RPE-specific) Vegfa had greatly reduced subretinal infiltration of microglia/macrophages, subsequently reducing neovascular tufts. These findings highlight the contribution of microglia/macrophages to the pathogenesis of neovascularization, provide valuable clues regarding potential causative cellular mechanisms for subretinal neovascularization in patients with MacTel and RAP and suggest that targeting microglia activation may be a therapeutic option in these diseases.
视网膜下新生血管异常是威胁视力的视网膜疾病的特征,包括黄斑毛细血管扩张症(MacTel)和视网膜血管瘤样增生(RAP)。在极低密度脂蛋白受体(Vldlr-/-)突变小鼠中观察到视网膜下新生血管丛和光感受器功能障碍。这些变化反映了在 MacTel 和 RAP 患者中观察到的变化,但发病机制在很大程度上尚不清楚。在这项研究中,我们表明,视网膜小胶质细胞与 Vldlr-/- 小鼠和 MacTel 患者的视网膜组织中的视网膜新生血管丛密切相关;小胶质细胞/巨噬细胞的消融可显著阻止视网膜新生血管丛的形成,并改善电生理视网膜电图评估的神经元功能。具有视网膜色素上皮特异性(RPE 特异性)Vegfa 的 Vldlr-/- 小鼠的视网膜下小胶质细胞/巨噬细胞浸润大大减少,随后减少了新生血管丛。这些发现强调了小胶质细胞/巨噬细胞在新生血管形成发病机制中的作用,为 MacTel 和 RAP 患者视网膜下新生血管形成的潜在因果细胞机制提供了有价值的线索,并表明靶向小胶质细胞激活可能是这些疾病的一种治疗选择。